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Tag: dystrophy
PTC Therapeutics Begins Rolling NDA Submission To The FDA For Translarna To Treat Duchenne Muscular Dystrophy
2014-12-29 01:59:52| drugdiscoveryonline Home Page
PTC Therapeutics, Inc. (NASDAQ: PTCT) today announced that it has commenced a rolling submission of a New Drug Application (NDA) to the United States Food and Drug Administration (FDA) for Translarna™ for the treatment of nonsense mutation Duchenne muscular dystrophy (nmDMD)
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begins
rolling
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Isis Pharmaceuticals begins ISIS-DMPK Rx Phase 1 study for treatment of Myotonic Dystrophy Type 1
2014-06-10 09:16:58| Biotech - Topix.net
Isis Pharmaceuticals, Inc. announced today that it has initiated a Phase 1 study for ISIS-DMPKRx.
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study
treatment
phase
'CureDuchenne Ventures' Launched To Accelerate Drug Discovery And Development For Duchenne Muscular Dystrophy
2013-10-02 05:57:32| drugdiscoveryonline News Articles
CureDuchenne announced today the launch of CureDuchenne Ventures, a new initiative to identify and develop a robust pipeline of therapies to treat Duchenne, the most common and lethal form of muscular dystrophy
Tags: development
drug
discovery
launched
GSK, Prosensa muscular dystrophy drug misses study goal
2013-09-20 17:19:30| Biotech - Topix.net
An experimental drug for Duchenne muscular dystrophy from GlaxoSmithKline and Prosensa failed to meet its goal in a late-stage clinical trial, sending shares in Prosensa tumbling 75 percent in pre-market trade.
Tags: study
goal
drug
muscular
Muscular Dystrophy campaign helping thousands
2013-08-18 23:59:28| Grocery - Topix.net
Allan Voykin, center, his wife Tamara, fourth from right, and their three sons pose for a group shot with Safeway staff members in Castlegar on Sunday, Aug. 18. The awareness weekend for the 'Make Muscles Move' campaign encourages donations to help with neuromuscular research and mobility grants for those with Muscular Dystrophy.
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